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598 lines
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117 KiB
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<div class="search"><div class="search_form"><label for="database" class="offscreen_noflow">Search database</label><select id="database"><optgroup label="Recent"><option value="pmc" selected="selected" data-ac_dict="pmc-search-autocomplete">PMC</option><option value="books">Books</option><option value="nuccore">Nucleotide</option><option value="sra" class="last">SRA</option></optgroup><optgroup label="All"><option value="gquery">All Databases</option><option value="assembly">Assembly</option><option value="biocollections">Biocollections</option><option value="bioproject">BioProject</option><option value="biosample">BioSample</option><option value="books">Books</option><option value="clinvar">ClinVar</option><option value="cdd">Conserved Domains</option><option value="gap">dbGaP</option><option value="dbvar">dbVar</option><option value="gene">Gene</option><option value="genome">Genome</option><option value="gds">GEO DataSets</option><option value="geoprofiles">GEO Profiles</option><option value="gtr">GTR</option><option value="ipg">Identical Protein Groups</option><option value="medgen" data-ac_dict="medgen_disease_name">MedGen</option><option value="mesh" data-ac_dict="mesh_suggestions">MeSH</option><option value="nlmcatalog">NLM Catalog</option><option value="nuccore">Nucleotide</option><option value="omim">OMIM</option><option value="pmc" data-ac_dict="pmc-search-autocomplete">PMC</option><option value="protein">Protein</option><option value="proteinclusters">Protein Clusters</option><option value="protfam">Protein Family Models</option><option value="pcassay">PubChem BioAssay</option><option value="pccompound">PubChem Compound</option><option value="pcsubstance">PubChem Substance</option><option value="pubmed" data-ac_dict="pm_related_queries_2">PubMed</option><option value="snp">SNP</option><option value="sra">SRA</option><option value="structure">Structure</option><option value="taxonomy">Taxonomy</option><option value="toolkit">ToolKit</option><option value="toolkitall">ToolKitAll</option><option value="toolkitbookgh">ToolKitBookgh</option></optgroup></select><div class="nowrap"><label for="term" class="offscreen_noflow" accesskey="/">Search term</label><div class="nowrap"><input type="text" name="term" id="term" title="Search PMC. Use up and down arrows to choose an item from the autocomplete." value=""Mol Ther Nucleic Acids"[jour]" class="jig-ncbiclearbutton jig-ncbiautocomplete" data-jigconfig="dictionary:'pmc-search-autocomplete',disableUrl:'NcbiSearchBarAutoComplCtrl'" autocomplete="off" data-sbconfig="ds:'no',pjs:'yes',afs:'yes'" /></div><button id="search" type="submit" class="button_search nowrap" cmd="go">Search</button></div></div><ul class="searchlinks inline_list"><set></set><li><a name="SaveSearch" title="Click to create an email alert for this search" href="/sites/myncbi/searches/save?db=pmc&qk=86291" id="SaveSearch">Create alert</a></li><li><a href="/pmc/journals/">Journal List</a></li><li><a href="/pmc/advanced">Advanced</a></li><li class="help"><a id="help" class="jig-ncbihelpwindow" target="ncbihelp" name="help" href="/books/NBK3825">Help</a></li></ul></div>
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<div><input name="EntrezSystem2.PEntrez.PMC.Pmc_ResultsPanel.EmailTab.EmailReport" sid="1" type="hidden" /><input name="EntrezSystem2.PEntrez.PMC.Pmc_ResultsPanel.EmailTab.EmailFormat" sid="1" type="hidden" /><input name="EntrezSystem2.PEntrez.PMC.Pmc_ResultsPanel.EmailTab.EmailCount" sid="1" type="hidden" /><input name="EntrezSystem2.PEntrez.PMC.Pmc_ResultsPanel.EmailTab.EmailStart" sid="1" type="hidden" /><input name="EntrezSystem2.PEntrez.PMC.Pmc_ResultsPanel.EmailTab.EmailSort" sid="1" type="hidden" /><input name="EntrezSystem2.PEntrez.PMC.Pmc_ResultsPanel.EmailTab.Email" sid="1" type="hidden" /><input name="EntrezSystem2.PEntrez.PMC.Pmc_ResultsPanel.EmailTab.EmailSubject" sid="1" type="hidden" /><input name="EntrezSystem2.PEntrez.PMC.Pmc_ResultsPanel.EmailTab.EmailText" sid="1" type="hidden" /><input name="EntrezSystem2.PEntrez.PMC.Pmc_ResultsPanel.EmailTab.EmailQueryKey" sid="1" type="hidden" /><input name="EntrezSystem2.PEntrez.PMC.Pmc_ResultsPanel.EmailTab.EmailHID" sid="1" type="hidden" value="14AdQTBsHEYfX0Y9CX5_9UIZUHPMH2mozR77jkdcrd" /><input name="EntrezSystem2.PEntrez.PMC.Pmc_ResultsPanel.EmailTab.QueryDescription" sid="1" type="hidden" /><input name="EntrezSystem2.PEntrez.PMC.Pmc_ResultsPanel.EmailTab.Key" sid="1" type="hidden" /><input name="EntrezSystem2.PEntrez.PMC.Pmc_ResultsPanel.EmailTab.Answer" sid="1" type="hidden" /><input name="EntrezSystem2.PEntrez.PMC.Pmc_ResultsPanel.EmailTab.Holding" sid="1" type="hidden" value="" /><input name="EntrezSystem2.PEntrez.PMC.Pmc_ResultsPanel.EmailTab.HoldingFft" sid="1" type="hidden" value="" /><input name="EntrezSystem2.PEntrez.PMC.Pmc_ResultsPanel.EmailTab.HoldingNdiSet" sid="1" type="hidden" value="" /><input name="EntrezSystem2.PEntrez.PMC.Pmc_ResultsPanel.EmailTab.OToolValue" sid="1" type="hidden" value="" /><input name="EntrezSystem2.PEntrez.PMC.Pmc_ResultsPanel.EmailTab.SubjectList" sid="1" type="hidden" value="" /></div><!-- hidden inputs -->
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<div id="faceted_search" class="col two_col">
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<h2 class="offscreen_noflow">Result Filters</h2>
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<div class="facet_cont" data-db="pmc" data-default_grps="fg_types,fg_text_availability,fg_pubdate,fg_funding" data-sd="db:'pmc',op:'search',term:'%22Mol%20Ther%20Nucleic%20Acids%22%5Bjour%5D',qk:'86291',linkname:'',idsfromresult:'',extra:''"><ul class="facet" data-filter_id="types" id="_types"><li class="filter_grp "><div class="clearfix"><h3>Article attributes</h3><a href="#" data-value_id="" class="clear clear_hide">Clear</a></div><ul><li class="fil_val"><a href="#" data-value_id="associateddata">Associated Data</a></li><li class="fil_val"><a href="#" data-value_id="manuscripts">Author manuscripts</a></li><li class="fil_val"><a href="#" data-value_id="digitazed">Digitized back issues</a></li><li class="fil_val"><a href="#" data-value_id="medline">MEDLINE journals</a></li><li class="fil_val"><a href="#" data-value_id="openaccess">Open access</a></li><li class="fil_val"><a href="#" data-value_id="preprint">Preprints</a></li><li class="fil_val"><a href="#" data-value_id="retracted">Retracted</a></li></ul></li></ul><ul class="facet" data-filter_id="text_availability" id="_text_availability"><li class="filter_grp "><div class="clearfix"><h3>Text availability</h3><a href="#" data-value_id="" class="clear clear_hide">Clear</a></div><ul><li class="fil_val"><a href="#" data-value_id="embargoed">Include embargoed articles</a></li></ul></li></ul><ul class="facet" data-filter_id="pubdate" data-ds="yes" id="_pubdate"><li class="filter_grp"><div class="clearfix"><h3>Publication date</h3><a href="#" data-value_id="" class="clear clear_hide">clear</a></div><ul><li class="fil_val"><a href="#" data-value_id="y_1">1 year</a></li><li class="fil_val"><a href="#" data-value_id="y_5">5 years</a></li><li class="fil_val"><a href="#" data-value_id="y_10">10 years</a></li><li class="daterange"><a id="facet_date_rangepubdate" href="#facet_date_range_divpubdate" class="jig-ncbipopper" data-jigconfig="triggerPosition: 'middle right', destPosition: 'middle left', hasArrow: true, arrowDirection: 'left', closeEvent : 'click', openEvent: 'click', adjustFit: 'autoAdjust', openAnimation: 'none', closeAnimation: 'none', addCloseButton:true, width: '375px'">
|
||
Custom range...</a></li><div id="facet_date_range_divpubdate" style="display:none;" class="facets_dialog"><button class="ui-ncbipopper-close-button ui-ncbipopper-close-button-generated ui-state-default ui-corner-all ui-button-text-only ui-ncbibutton ui-ncbibutton-blue" generated="true" role="button" aria-disabled="false"><span class="ui-button-text">x</span></button><h4>Custom date range</h4><div><label class="offscreen_noflow" for="facet_date_st_yearpubdate">Start Year</label><input type="text" size="4" placeholder="YYYY" id="facet_date_st_yearpubdate" value="" class="input_date_ym" /><label class="offscreen_noflow" for="facet_date_st_monthpubdate">Start Month</label><input type="text" size="2" placeholder="MM" id="facet_date_st_monthpubdate" value="" class="input_date_ym" /><label class="offscreen_noflow" for="facet_date_st_daypubdate">Start Day</label><input type="text" size="2" placeholder="DD" id="facet_date_st_daypubdate" value="" /><span>to</span><label class="offscreen_noflow" for="facet_date_end_yearpubdate">End Year</label><input type="text" size="4" placeholder="YYYY" id="facet_date_end_yearpubdate" value="" class="input_date_ym" /><label class="offscreen_noflow" for="facet_date_end_monthpubdate">End Month</label><input type="text" size="2" placeholder="MM" id="facet_date_end_monthpubdate" value="" class="input_date_ym" /><label class="offscreen_noflow" for="facet_date_end_daypubdate">End Day</label><input type="text" size="2" placeholder="DD" id="facet_date_end_daypubdate" value="" /></div><div class="actions clearfix"><button class="jig-ncbibutton primary-action btn_date_apply" data-jigconfig="'color': 'ui-ncbibutton-blue'" id="facet_date_range_applypubdate">Apply</button><button class="jig-ncbibutton secondary-action btn_date_clear" data-jigconfig="'color': 'ui-ncbibutton-gray'" id="facet_date_range_clearpubdate">Clear</button></div></div></ul></li></ul><ul class="facet" data-filter_id="funding" id="_funding"><li class="filter_grp "><div class="clearfix"><h3>Research Funder</h3><a href="#" data-value_id="" class="clear clear_hide">Clear</a></div><ul><li class="fil_val"><a href="#" data-value_id="funder_nih">NIH</a></li><li class="fil_val"><a href="#" data-value_id="funder_ahrq">AHRQ</a></li><li class="fil_val"><a href="#" data-value_id="funder_acl">ACL</a></li><li class="fil_val"><a href="#" data-value_id="funder_aspr">ASPR</a></li><li class="fil_val"><a href="#" data-value_id="funder_cdc">CDC</a></li><li class="fil_val"><a href="#" data-value_id="funder_dhs">DHS</a></li><li class="fil_val"><a href="#" data-value_id="funder_epa">EPA</a></li><li class="fil_val"><a href="#" data-value_id="funder_fda">FDA</a></li><li class="fil_val"><a href="#" data-value_id="funder_nasa">NASA</a></li><li class="fil_val"><a href="#" data-value_id="funder_nist">NIST</a></li><li class="fil_val"><a href="#" data-value_id="funder_va">VA</a></li><li class="more"><a href="#funding_more" data-value_id="fetch_more" data-jigconfig=" hasArrow: true, arrowDirection: 'left', closeEvent : 'click', openEvent: 'click', adjustFit: 'autoAdjust', openAnimation: 'none', closeAnimation: 'none', addCloseButton:true, width: '300px'">Customize ...</a><div style="display:none;" id="funding_more"></div></li></ul></li></ul><ul class="facet facet_reset"><li><a href="#" data-value_id="reset">Clear all</a></li></ul><ul class="facet_tools"><li><a id="more_filter_groups_link" href="#more_filter_groups" class="jig-ncbipopper" data-jigconfig="triggerPosition: 'middle right', destPosition: 'top left', hasArrow: true, arrowDirection: 'left', closeEvent : 'click', openEvent: 'click', adjustFit: 'autoAdjust', openAnimation: 'none', closeAnimation: 'none', addCloseButton:true, width: '180px'">
|
||
Show additional filters</a></li><div id="more_filter_groups" style="display:none;" class="facets_dialog"><button class="ui-ncbipopper-close-button ui-ncbipopper-close-button-generated ui-state-default ui-corner-all ui-button-text-only ui-ncbibutton ui-ncbibutton-blue" generated="true" role="button" aria-disabled="false"><span class="ui-button-text">x</span></button><h4>Additional filters</h4><ul class="filter_groups_more facet"><li><input type="checkbox" id="fg_types" /><label for="fg_types">Article attributes</label></li><li><input type="checkbox" id="fg_text_availability" /><label for="fg_text_availability">Text availability</label></li><li><input type="checkbox" id="fg_pubdate" data-always_show="yes" /><label for="fg_pubdate">Publication date</label></li><li><input type="checkbox" id="fg_funding" data-always_show="yes" /><label for="fg_funding">Research Funder</label></li><li><input id="fg_field_search" type="checkbox" /><label for="fg_field_search">Search fields</label></li></ul><div class="actions clearfix"><button class="filter_groups_more_apply jig-ncbibutton primary-action" id="filter_groups_apply" data-jigconfig="'color': 'ui-ncbibutton-blue'">Show</button></div></div></ul><input name="EntrezSystem2.PEntrez.PMC.Facets.FacetsUrlFrag" sid="1" type="hidden" value="filters=" /><input name="EntrezSystem2.PEntrez.PMC.Facets.FacetSubmitted" sid="1" type="hidden" value="false" /><input name="EntrezSystem2.PEntrez.PMC.Facets.BMFacets" sid="1" type="hidden" value="" /></div>
|
||
</div>
|
||
<div id="maincontent" class="col seven_col">
|
||
<div class="content">
|
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<div class="results_settings"><h4 class="left display_settings content_header jig-ncbipopper" id="display_set" data-jigconfig="triggerPosition : 'bottom center',destPosition : 'top center',destSelector : '#display_settings_menu', hasArrow : false,openEvent : 'click',closeEvent : 'click',isTriggerElementCloseClick: false,addCloseButton : true, multipleHandlesSelector:'#display_set ~ ul.display_settings a', groupName: 'entrez_pg'"><a href="#" class="tgt_dark">Display Settings:</a></h4><ul class="inline_list left display_settings"><li><a name="EntrezSystem2.PEntrez.PMC.Pmc_ResultsPanel.Pmc_DisplayBar.Display" sid="2" href="#" sourceContent="display_settings_menu" id="EntrezSystem2.PEntrez.PMC.Pmc_ResultsPanel.Pmc_DisplayBar.Display">Summary,</a></li><li><a name="EntrezSystem2.PEntrez.PMC.Pmc_ResultsPanel.Pmc_DisplayBar.Display" sid="3" href="#" sourceContent="display_settings_menu" id="EntrezSystem2.PEntrez.PMC.Pmc_ResultsPanel.Pmc_DisplayBar.Display">20 per page,</a></li><li><a name="EntrezSystem2.PEntrez.PMC.Pmc_ResultsPanel.Pmc_DisplayBar.Display" sid="4" href="#" sourceContent="display_settings_menu" id="EntrezSystem2.PEntrez.PMC.Pmc_ResultsPanel.Pmc_DisplayBar.Display">Sorted by Default order</a></li></ul><div id="display_settings_menu" class="disp_settings tabPopper"><fieldset class="format"><legend>Format</legend><ul class="column_list"><li><input type="radio" name="EntrezSystem2.PEntrez.PMC.Pmc_ResultsPanel.Pmc_DisplayBar.sPresentation" sid="1" value="DocSum" format="" id="DocSum" checked="true" /><label for="DocSum">Summary</label></li><li><input type="radio" name="EntrezSystem2.PEntrez.PMC.Pmc_ResultsPanel.Pmc_DisplayBar.sPresentation" sid="2" value="DocSum" format="text" id="DocSumtext" /><label for="DocSumtext">Summary (text)</label></li><li><input type="radio" name="EntrezSystem2.PEntrez.PMC.Pmc_ResultsPanel.Pmc_DisplayBar.sPresentation" sid="3" value="MEDLINE" format="text" id="MEDLINEtext" /><label for="MEDLINEtext">MEDLINE</label></li><li><input type="radio" name="EntrezSystem2.PEntrez.PMC.Pmc_ResultsPanel.Pmc_DisplayBar.sPresentation" sid="4" value="uilist" format="text" id="uilisttext" /><label for="uilisttext">PMCID List</label></li></ul></fieldset><fieldset class="items"><legend>Items per page</legend><ul class="column_list"><li><input type="radio" name="EntrezSystem2.PEntrez.PMC.Pmc_ResultsPanel.Pmc_DisplayBar.sPageSize" sid="1" value="5" id="ps5" /><label for="ps5">5</label></li><li><input type="radio" name="EntrezSystem2.PEntrez.PMC.Pmc_ResultsPanel.Pmc_DisplayBar.sPageSize" sid="2" value="10" id="ps10" /><label for="ps10">10</label></li><li><input type="radio" name="EntrezSystem2.PEntrez.PMC.Pmc_ResultsPanel.Pmc_DisplayBar.sPageSize" sid="3" value="20" id="ps20" checked="true" /><label for="ps20">20</label></li><li><input type="radio" name="EntrezSystem2.PEntrez.PMC.Pmc_ResultsPanel.Pmc_DisplayBar.sPageSize" sid="4" value="50" id="ps50" /><label for="ps50">50</label></li><li><input type="radio" name="EntrezSystem2.PEntrez.PMC.Pmc_ResultsPanel.Pmc_DisplayBar.sPageSize" sid="5" value="100" id="ps100" /><label for="ps100">100</label></li></ul></fieldset><fieldset class="sort"><legend>Sort by</legend><ul class="column_list"><li><input type="radio" name="EntrezSystem2.PEntrez.PMC.Pmc_ResultsPanel.Pmc_DisplayBar.sSort" sid="1" value="none" id="none" checked="true" /><label for="none">Default order</label></li><li><input type="radio" name="EntrezSystem2.PEntrez.PMC.Pmc_ResultsPanel.Pmc_DisplayBar.sSort" sid="2" value="PubDate" id="PubDate" /><label for="PubDate">Pub Date</label></li><li><input type="radio" name="EntrezSystem2.PEntrez.PMC.Pmc_ResultsPanel.Pmc_DisplayBar.sSort" sid="3" value="Journal" id="Journal" /><label for="Journal">Journal</label></li><li><input type="radio" name="EntrezSystem2.PEntrez.PMC.Pmc_ResultsPanel.Pmc_DisplayBar.sSort" sid="4" value="PmcLiveDate" id="PmcLiveDate" /><label for="PmcLiveDate">PMC Live Date</label></li></ul></fieldset><button name="EntrezSystem2.PEntrez.PMC.Pmc_ResultsPanel.Pmc_DisplayBar.SetDisplay" sid="1" class="button_apply ncbipopper-close-button">Apply</button></div><h4 class="content_header send_to align_right jig-ncbipopper" id="sendto" data-jigconfig="triggerPosition:'bottom center', destPosition : 'top center',destSelector : '#send_to_menu', hasArrow : false, openEvent : 'click',closeEvent : 'click', isTriggerElementCloseClick: false, addCloseButton:true, groupName: 'entrez_pg', adjustFit:'none'"><a href="#" sourceContent="send_to_menu" class="tgt_dark">Send to:</a><script type="text/javascript">
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jQuery(document).ready( function () {
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jQuery("#send_to_menu input[type='radio']").click( function () {
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<div><div class="rprt"><div class="rprtnum"><label for="UidCheckBox11919288" class="ui-helper-hidden-accessible">Select item 11919288</label><input name="EntrezSystem2.PEntrez.PMC.Pmc_ResultsPanel.Pmc_RVDocSum.uid" sid="1" type="checkbox" id="UidCheckBox11919288" value="11919288" /><span>1.</span></div><div class="rslt"><div class="title"><a ref="ordinalpos=1&ncbi_uid=11919288&link_uid=11919288&linksrc=docsum_title" href="https://pmc.ncbi.nlm.nih.gov/articles/PMC11919288/" class="view">Impact on efficacy of target reduction of two FDA-approved ASO drugs by intracellular glucose levels in <em>in vitro</em> cell models</a></div><div class="supp"><div class="desc">Le Tra Giang Nguyen, Sherouk M. Tawfik, Jing Jin, Andrea Durwin, Xiao-bo Zhong</div><div class="details"><b>Mol Ther Nucleic Acids</b>. <span class="citation-publication-date">2025 Mar 11; </span>36(1): 102487. <span class="">Published online 2025 Feb 15. </span><span class="doi"><span>doi: </span>10.1016/j.omtn.2025.102487</span></div></div><div class="aux"><div class="resc"><dl class="rprtid"><dt>PMCID: </dt><dd>PMC11919288</dd></dl></div></div><div class="aux"><div class="links"><a ref="ordinalpos=1&ncbi_uid=11919288&link_uid=11919288&linksrc=docsum_title" class="view" href="https://pmc.ncbi.nlm.nih.gov/articles/PMC11919288/">Article</a><a ref="ordinalpos=1&ncbi_uid=11919288&link_uid=11919288&linksrc=docsum_title" class="view" href="https://pmc.ncbi.nlm.nih.gov/articles/PMC11919288/pdf/main.pdf">PDF–4.2M</a></div></div></div></div><div class="rprt"><div class="rprtnum"><label for="UidCheckBox11905888" class="ui-helper-hidden-accessible">Select item 11905888</label><input name="EntrezSystem2.PEntrez.PMC.Pmc_ResultsPanel.Pmc_RVDocSum.uid" sid="2" type="checkbox" id="UidCheckBox11905888" value="11905888" /><span>2.</span></div><div class="rslt"><div class="title"><a ref="ordinalpos=2&ncbi_uid=11905888&link_uid=11905888&linksrc=docsum_title" href="https://pmc.ncbi.nlm.nih.gov/articles/PMC11905888/" class="view"><em>In vivo</em> efficacy and safety of systemically administered serinol nucleic acid-modified antisense oligonucleotides in mouse kidney</a></div><div class="supp"><div class="desc">Toshiki Tsuboi, Keita Hattori, Takuji Ishimoto, Kentaro Imai, Tomohito Doke, Junichiro Hagita, Jumpei Ariyoshi, Kazuhiro Furuhashi, Noritoshi Kato, Yasuhiko Ito, Yukiko Kamiya, Hiroyuki Asanuma, Shoichi Maruyama</div><div class="details"><b>Mol Ther Nucleic Acids</b>. <span class="citation-publication-date">2025 Mar 11; </span>36(1): 102497. <span class="">Published online 2025 Feb 25. </span><span class="doi"><span>doi: </span>10.1016/j.omtn.2025.102497</span></div><div class="details"><dl><dt class="strong">Corrects: </dt><dd><a ref="ordinalpos=2&ncbi_uid=11905888&link_uid=11905888&linksrc=docsum_title" href="https://pmc.ncbi.nlm.nih.gov/articles/PMC11754010/"><span class="correction-info"><b>Mol Ther Nucleic Acids</b>. 2025 Mar 11; 36(1): 102387. </span></a></dd></dl></div></div><div class="aux"><div class="resc"><dl class="rprtid"><dt>PMCID: </dt><dd>PMC11905888</dd></dl></div></div><div class="aux"><div class="links"><a ref="ordinalpos=2&ncbi_uid=11905888&link_uid=11905888&linksrc=docsum_title" class="view" href="https://pmc.ncbi.nlm.nih.gov/articles/PMC11905888/">Correction</a><a ref="ordinalpos=2&ncbi_uid=11905888&link_uid=11905888&linksrc=docsum_title" class="view" href="https://pmc.ncbi.nlm.nih.gov/articles/PMC11905888/pdf/main.pdf">PDF–165K</a></div></div></div></div><div class="rprt"><div class="rprtnum"><label for="UidCheckBox11889969" class="ui-helper-hidden-accessible">Select item 11889969</label><input name="EntrezSystem2.PEntrez.PMC.Pmc_ResultsPanel.Pmc_RVDocSum.uid" sid="3" type="checkbox" id="UidCheckBox11889969" value="11889969" /><span>3.</span></div><div class="rslt"><div class="title"><a ref="ordinalpos=3&ncbi_uid=11889969&link_uid=11889969&linksrc=docsum_title" href="https://pmc.ncbi.nlm.nih.gov/articles/PMC11889969/" class="view">Unlocking the potential of allele-specific siRNA therapy: A novel approach for Crouzon syndrome</a></div><div class="supp"><div class="desc">Federico Di Rocco, Camilla de Laurentis</div><div class="details"><b>Mol Ther Nucleic Acids</b>. <span class="citation-publication-date">2025 Mar 11; </span>36(1): 102484. <span class="">Published online 2025 Feb 21. </span><span class="doi"><span>doi: </span>10.1016/j.omtn.2025.102484</span></div></div><div class="aux"><div class="resc"><dl class="rprtid"><dt>PMCID: </dt><dd>PMC11889969</dd></dl></div></div><div class="aux"><div class="links"><a ref="ordinalpos=3&ncbi_uid=11889969&link_uid=11889969&linksrc=docsum_title" class="view" href="https://pmc.ncbi.nlm.nih.gov/articles/PMC11889969/">Article</a><a ref="ordinalpos=3&ncbi_uid=11889969&link_uid=11889969&linksrc=docsum_title" class="view" href="https://pmc.ncbi.nlm.nih.gov/articles/PMC11889969/pdf/main.pdf">PDF–188K</a></div></div></div></div><div class="rprt"><div class="rprtnum"><label for="UidCheckBox11889949" class="ui-helper-hidden-accessible">Select item 11889949</label><input name="EntrezSystem2.PEntrez.PMC.Pmc_ResultsPanel.Pmc_RVDocSum.uid" sid="4" type="checkbox" id="UidCheckBox11889949" value="11889949" /><span>4.</span></div><div class="rslt"><div class="title"><a ref="ordinalpos=4&ncbi_uid=11889949&link_uid=11889949&linksrc=docsum_title" href="https://pmc.ncbi.nlm.nih.gov/articles/PMC11889949/" class="view">Unlocking RNA mysteries: Predicting subcellular localizations with AI</a></div><div class="supp"><div class="desc">Nguyen Quoc Khanh Le</div><div class="details"><b>Mol Ther Nucleic Acids</b>. <span class="citation-publication-date">2025 Mar 11; </span>36(1): 102481. <span class="">Published online 2025 Feb 21. </span><span class="doi"><span>doi: </span>10.1016/j.omtn.2025.102481</span></div></div><div class="aux"><div class="resc"><dl class="rprtid"><dt>PMCID: </dt><dd>PMC11889949</dd></dl></div></div><div class="aux"><div class="links"><a ref="ordinalpos=4&ncbi_uid=11889949&link_uid=11889949&linksrc=docsum_title" class="view" href="https://pmc.ncbi.nlm.nih.gov/articles/PMC11889949/">Article</a><a ref="ordinalpos=4&ncbi_uid=11889949&link_uid=11889949&linksrc=docsum_title" class="view" href="https://pmc.ncbi.nlm.nih.gov/articles/PMC11889949/pdf/main.pdf">PDF–1.6M</a></div></div></div></div><div class="rprt"><div class="rprtnum"><label for="UidCheckBox11903799" class="ui-helper-hidden-accessible">Select item 11903799</label><input name="EntrezSystem2.PEntrez.PMC.Pmc_ResultsPanel.Pmc_RVDocSum.uid" sid="5" type="checkbox" id="UidCheckBox11903799" value="11903799" /><span>5.</span></div><div class="rslt"><div class="title"><a ref="ordinalpos=5&ncbi_uid=11903799&link_uid=11903799&linksrc=docsum_title" href="https://pmc.ncbi.nlm.nih.gov/articles/PMC11903799/" class="view">Rescue of the disease-associated phenotype in CRISPR-corrected hiPSCs as a therapeutic approach for inherited retinal dystrophies</a></div><div class="supp"><div class="desc">Laura Siles, Esther Pomares</div><div class="details"><b>Mol Ther Nucleic Acids</b>. <span class="citation-publication-date">2025 Mar 11; </span>36(1): 102482. <span class="">Published online 2025 Feb 11. </span><span class="doi"><span>doi: </span>10.1016/j.omtn.2025.102482</span></div></div><div class="aux"><div class="resc"><dl class="rprtid"><dt>PMCID: </dt><dd>PMC11903799</dd></dl></div></div><div class="aux"><div class="links"><a ref="ordinalpos=5&ncbi_uid=11903799&link_uid=11903799&linksrc=docsum_title" class="view" href="https://pmc.ncbi.nlm.nih.gov/articles/PMC11903799/">Article</a><a ref="ordinalpos=5&ncbi_uid=11903799&link_uid=11903799&linksrc=docsum_title" class="view" href="https://pmc.ncbi.nlm.nih.gov/articles/PMC11903799/pdf/main.pdf">PDF–3.6M</a></div></div></div></div><div class="rprt"><div class="rprtnum"><label for="UidCheckBox11889396" class="ui-helper-hidden-accessible">Select item 11889396</label><input name="EntrezSystem2.PEntrez.PMC.Pmc_ResultsPanel.Pmc_RVDocSum.uid" sid="6" type="checkbox" id="UidCheckBox11889396" value="11889396" /><span>6.</span></div><div class="rslt"><div class="title"><a ref="ordinalpos=6&ncbi_uid=11889396&link_uid=11889396&linksrc=docsum_title" href="https://pmc.ncbi.nlm.nih.gov/articles/PMC11889396/" class="view">Potential ASO-based personalized treatment for Charcot-Marie-Tooth disease type 2S</a></div><div class="supp"><div class="desc">Sandra Smieszek, Bartlomiej Przychodzen, Christina Tyner, Caroline Johnson, Haimeng Bai, Jennifer M. Kwon, D. Walker Hagan, Caitlyn Niccum, Rocky Brighton, Kenneth Hawkins, Romy Aiken, Ahmad Nawaz, Xiufang Guo, James Hickman, Christos M. Polymeropoulos, Gunther Birznieks, Mihael H. Polymeropoulos</div><div class="details"><b>Mol Ther Nucleic Acids</b>. <span class="citation-publication-date">2025 Mar 11; </span>36(1): 102479. <span class="">Published online 2025 Feb 4. </span><span class="doi"><span>doi: </span>10.1016/j.omtn.2025.102479</span></div></div><div class="aux"><div class="resc"><dl class="rprtid"><dt>PMCID: </dt><dd>PMC11889396</dd></dl></div></div><div class="aux"><div class="links"><a ref="ordinalpos=6&ncbi_uid=11889396&link_uid=11889396&linksrc=docsum_title" class="view" href="https://pmc.ncbi.nlm.nih.gov/articles/PMC11889396/">Article</a><a ref="ordinalpos=6&ncbi_uid=11889396&link_uid=11889396&linksrc=docsum_title" class="view" href="https://pmc.ncbi.nlm.nih.gov/articles/PMC11889396/pdf/main.pdf">PDF–4.4M</a></div></div></div></div><div class="rprt"><div class="rprtnum"><label for="UidCheckBox11875208" class="ui-helper-hidden-accessible">Select item 11875208</label><input name="EntrezSystem2.PEntrez.PMC.Pmc_ResultsPanel.Pmc_RVDocSum.uid" sid="7" type="checkbox" id="UidCheckBox11875208" value="11875208" /><span>7.</span></div><div class="rslt"><div class="title"><a ref="ordinalpos=7&ncbi_uid=11875208&link_uid=11875208&linksrc=docsum_title" href="https://pmc.ncbi.nlm.nih.gov/articles/PMC11875208/" class="view">Effect of chemical modification on the exon-skipping activity of heteroduplex oligonucleotides</a></div><div class="supp"><div class="desc">Takenori Shimo, Juri Hasegawa, Kotaro Yoshioka, Yusuke Nakatsuji, Kotomi Aso, Keisuke Tachibana, Tetsuya Nagata, Takanori Yokota, Satoshi Obika</div><div class="details"><b>Mol Ther Nucleic Acids</b>. <span class="citation-publication-date">2025 Mar 11; </span>36(1): 102468. <span class="">Published online 2025 Feb 1. </span><span class="doi"><span>doi: </span>10.1016/j.omtn.2025.102468</span></div></div><div class="aux"><div class="resc"><dl class="rprtid"><dt>PMCID: </dt><dd>PMC11875208</dd></dl></div></div><div class="aux"><div class="links"><a ref="ordinalpos=7&ncbi_uid=11875208&link_uid=11875208&linksrc=docsum_title" class="view" href="https://pmc.ncbi.nlm.nih.gov/articles/PMC11875208/">Article</a><a ref="ordinalpos=7&ncbi_uid=11875208&link_uid=11875208&linksrc=docsum_title" class="view" href="https://pmc.ncbi.nlm.nih.gov/articles/PMC11875208/pdf/main.pdf">PDF–3.7M</a></div></div></div></div><div class="rprt"><div class="rprtnum"><label for="UidCheckBox11875178" class="ui-helper-hidden-accessible">Select item 11875178</label><input name="EntrezSystem2.PEntrez.PMC.Pmc_ResultsPanel.Pmc_RVDocSum.uid" sid="8" type="checkbox" id="UidCheckBox11875178" value="11875178" /><span>8.</span></div><div class="rslt"><div class="title"><a ref="ordinalpos=8&ncbi_uid=11875178&link_uid=11875178&linksrc=docsum_title" href="https://pmc.ncbi.nlm.nih.gov/articles/PMC11875178/" class="view">i-Motifs as regulatory switches: Mechanisms and implications for gene expression</a></div><div class="supp"><div class="desc">Auroni Deep, Anjali Bhat, Vivekanandan Perumal, Saran Kumar</div><div class="details"><b>Mol Ther Nucleic Acids</b>. <span class="citation-publication-date">2025 Mar 11; </span>36(1): 102474. <span class="">Published online 2025 Feb 1. </span><span class="doi"><span>doi: </span>10.1016/j.omtn.2025.102474</span></div></div><div class="aux"><div class="resc"><dl class="rprtid"><dt>PMCID: </dt><dd>PMC11875178</dd></dl></div></div><div class="aux"><div class="links"><a ref="ordinalpos=8&ncbi_uid=11875178&link_uid=11875178&linksrc=docsum_title" class="view" href="https://pmc.ncbi.nlm.nih.gov/articles/PMC11875178/">Article</a><a ref="ordinalpos=8&ncbi_uid=11875178&link_uid=11875178&linksrc=docsum_title" class="view" href="https://pmc.ncbi.nlm.nih.gov/articles/PMC11875178/pdf/main.pdf">PDF–2.7M</a></div></div></div></div><div class="rprt"><div class="rprtnum"><label for="UidCheckBox11872078" class="ui-helper-hidden-accessible">Select item 11872078</label><input name="EntrezSystem2.PEntrez.PMC.Pmc_ResultsPanel.Pmc_RVDocSum.uid" sid="9" type="checkbox" id="UidCheckBox11872078" value="11872078" /><span>9.</span></div><div class="rslt"><div class="title"><a ref="ordinalpos=9&ncbi_uid=11872078&link_uid=11872078&linksrc=docsum_title" href="https://pmc.ncbi.nlm.nih.gov/articles/PMC11872078/" class="view">Enhanced HDR-mediated correction of heterozygous <em>COL7A1</em> mutations for recessive dystrophic epidermolysis bullosa</a></div><div class="supp"><div class="desc">John M.T. Hunt, Alex du Rand, Daniel Verdon, Leah Clemance, Evert Loef, Chloe Malhi, Ben Buttle, David J.H.F. Knapp, Yale S. Michaels, Jonathan Garlick, P. Rod Dunbar, Diana Purvis, Vaughan Feisst, Hilary Sheppard</div><div class="details"><b>Mol Ther Nucleic Acids</b>. <span class="citation-publication-date">2025 Mar 11; </span>36(1): 102472. <span class="">Published online 2025 Feb 1. </span><span class="doi"><span>doi: </span>10.1016/j.omtn.2025.102472</span></div></div><div class="aux"><div class="resc"><dl class="rprtid"><dt>PMCID: </dt><dd>PMC11872078</dd></dl></div></div><div class="aux"><div class="links"><a ref="ordinalpos=9&ncbi_uid=11872078&link_uid=11872078&linksrc=docsum_title" class="view" href="https://pmc.ncbi.nlm.nih.gov/articles/PMC11872078/">Article</a><a ref="ordinalpos=9&ncbi_uid=11872078&link_uid=11872078&linksrc=docsum_title" class="view" href="https://pmc.ncbi.nlm.nih.gov/articles/PMC11872078/pdf/main.pdf">PDF–4.2M</a></div></div></div></div><div class="rprt"><div class="rprtnum"><label for="UidCheckBox11869860" class="ui-helper-hidden-accessible">Select item 11869860</label><input name="EntrezSystem2.PEntrez.PMC.Pmc_ResultsPanel.Pmc_RVDocSum.uid" sid="10" type="checkbox" id="UidCheckBox11869860" value="11869860" /><span>10.</span></div><div class="rslt"><div class="title"><a ref="ordinalpos=10&ncbi_uid=11869860&link_uid=11869860&linksrc=docsum_title" href="https://pmc.ncbi.nlm.nih.gov/articles/PMC11869860/" class="view"><em>In vivo</em> production of engineered ACE2 decoy protects lungs from SARS-CoV-2 infection</a></div><div class="supp"><div class="desc">Yuta Suzuki, Takayuki Miyazaki, Yoko Ida, Tatsuya Suzuki, Yumi Itoh, Shuto Nakao, Keita Kondo, Kenji Kubara, Keisuke Nishioka, Hiroki Muto, Ryuji Watari, Toshifumi Hirayama, Dai Kakiuchi, Shinya Sato, Satoshi Inoue, Yoshifumi Uemoto, Yohei Mukai, Atsushi Hoshino, Toru Okamoto, Junji Matsui</div><div class="details"><b>Mol Ther Nucleic Acids</b>. <span class="citation-publication-date">2025 Mar 11; </span>36(1): 102467. <span class="">Published online 2025 Jan 29. </span><span class="doi"><span>doi: </span>10.1016/j.omtn.2025.102467</span></div></div><div class="aux"><div class="resc"><dl class="rprtid"><dt>PMCID: </dt><dd>PMC11869860</dd></dl></div></div><div class="aux"><div class="links"><a ref="ordinalpos=10&ncbi_uid=11869860&link_uid=11869860&linksrc=docsum_title" class="view" href="https://pmc.ncbi.nlm.nih.gov/articles/PMC11869860/">Article</a><a ref="ordinalpos=10&ncbi_uid=11869860&link_uid=11869860&linksrc=docsum_title" class="view" href="https://pmc.ncbi.nlm.nih.gov/articles/PMC11869860/pdf/main.pdf">PDF–4.5M</a></div></div></div></div><div class="rprt"><div class="rprtnum"><label for="UidCheckBox11847731" class="ui-helper-hidden-accessible">Select item 11847731</label><input name="EntrezSystem2.PEntrez.PMC.Pmc_ResultsPanel.Pmc_RVDocSum.uid" sid="11" type="checkbox" id="UidCheckBox11847731" value="11847731" /><span>11.</span></div><div class="rslt"><div class="title"><a ref="ordinalpos=11&ncbi_uid=11847731&link_uid=11847731&linksrc=docsum_title" href="https://pmc.ncbi.nlm.nih.gov/articles/PMC11847731/" class="view">Pan-cancer characterization of m6A-mediated regulation of T cell exhaustion dynamics and clinical relevancies in human cancers</a></div><div class="supp"><div class="desc">Weiping Ji, Ye Fang, Liwei Chen, Yitong Zheng, Yifei Pei, Changqiu Mei, Meng Zhou</div><div class="details"><b>Mol Ther Nucleic Acids</b>. <span class="citation-publication-date">2025 Mar 11; </span>36(1): 102465. <span class="">Published online 2025 Jan 25. </span><span class="doi"><span>doi: </span>10.1016/j.omtn.2025.102465</span></div></div><div class="aux"><div class="resc"><dl class="rprtid"><dt>PMCID: </dt><dd>PMC11847731</dd></dl></div></div><div class="aux"><div class="links"><a ref="ordinalpos=11&ncbi_uid=11847731&link_uid=11847731&linksrc=docsum_title" class="view" href="https://pmc.ncbi.nlm.nih.gov/articles/PMC11847731/">Article</a><a ref="ordinalpos=11&ncbi_uid=11847731&link_uid=11847731&linksrc=docsum_title" class="view" href="https://pmc.ncbi.nlm.nih.gov/articles/PMC11847731/pdf/main.pdf">PDF–4.7M</a></div></div></div></div><div class="rprt"><div class="rprtnum"><label for="UidCheckBox11848774" class="ui-helper-hidden-accessible">Select item 11848774</label><input name="EntrezSystem2.PEntrez.PMC.Pmc_ResultsPanel.Pmc_RVDocSum.uid" sid="12" type="checkbox" id="UidCheckBox11848774" value="11848774" /><span>12.</span></div><div class="rslt"><div class="title"><a ref="ordinalpos=12&ncbi_uid=11848774&link_uid=11848774&linksrc=docsum_title" href="https://pmc.ncbi.nlm.nih.gov/articles/PMC11848774/" class="view">TMEM97 governs partial epithelial-mesenchymal transition of retinal pigment epithelial cells via the CTNND2-ADAM10 axis</a></div><div class="supp"><div class="desc">Jing Li, Yosuke Nagasaka, Hongtao Shen, Xinyu Zhou, Jianjie Ma, Dilza Trevisan-Silva, Nicholas E. Sherman, Jayakrishna Ambati, Bradley D. Gelfand, Lian-Wang Guo</div><div class="details"><b>Mol Ther Nucleic Acids</b>. <span class="citation-publication-date">2025 Mar 11; </span>36(1): 102460. <span class="">Published online 2025 Jan 21. </span><span class="doi"><span>doi: </span>10.1016/j.omtn.2025.102460</span></div></div><div class="aux"><div class="resc"><dl class="rprtid"><dt>PMCID: </dt><dd>PMC11848774</dd></dl></div></div><div class="aux"><div class="links"><a ref="ordinalpos=12&ncbi_uid=11848774&link_uid=11848774&linksrc=docsum_title" class="view" href="https://pmc.ncbi.nlm.nih.gov/articles/PMC11848774/">Article</a><a ref="ordinalpos=12&ncbi_uid=11848774&link_uid=11848774&linksrc=docsum_title" class="view" href="https://pmc.ncbi.nlm.nih.gov/articles/PMC11848774/pdf/main.pdf">PDF–6.9M</a></div></div></div></div><div class="rprt"><div class="rprtnum"><label for="UidCheckBox11869866" class="ui-helper-hidden-accessible">Select item 11869866</label><input name="EntrezSystem2.PEntrez.PMC.Pmc_ResultsPanel.Pmc_RVDocSum.uid" sid="13" type="checkbox" id="UidCheckBox11869866" value="11869866" /><span>13.</span></div><div class="rslt"><div class="title"><a ref="ordinalpos=13&ncbi_uid=11869866&link_uid=11869866&linksrc=docsum_title" href="https://pmc.ncbi.nlm.nih.gov/articles/PMC11869866/" class="view">Engineering of SauriCas9 with enhanced specificity</a></div><div class="supp"><div class="desc">Xiaoqi Zhang, Chen Tao, Miaomiao Li, Sufang Zhang, Puping Liang, Yan Huang, Huihui Liu, Yongming Wang</div><div class="details"><b>Mol Ther Nucleic Acids</b>. <span class="citation-publication-date">2025 Mar 11; </span>36(1): 102455. <span class="">Published online 2025 Jan 17. </span><span class="doi"><span>doi: </span>10.1016/j.omtn.2025.102455</span></div></div><div class="aux"><div class="resc"><dl class="rprtid"><dt>PMCID: </dt><dd>PMC11869866</dd></dl></div></div><div class="aux"><div class="links"><a ref="ordinalpos=13&ncbi_uid=11869866&link_uid=11869866&linksrc=docsum_title" class="view" href="https://pmc.ncbi.nlm.nih.gov/articles/PMC11869866/">Article</a><a ref="ordinalpos=13&ncbi_uid=11869866&link_uid=11869866&linksrc=docsum_title" class="view" href="https://pmc.ncbi.nlm.nih.gov/articles/PMC11869866/pdf/main.pdf">PDF–3.7M</a></div></div></div></div><div class="rprt"><div class="rprtnum"><label for="UidCheckBox11847086" class="ui-helper-hidden-accessible">Select item 11847086</label><input name="EntrezSystem2.PEntrez.PMC.Pmc_ResultsPanel.Pmc_RVDocSum.uid" sid="14" type="checkbox" id="UidCheckBox11847086" value="11847086" /><span>14.</span></div><div class="rslt"><div class="title"><a ref="ordinalpos=14&ncbi_uid=11847086&link_uid=11847086&linksrc=docsum_title" href="https://pmc.ncbi.nlm.nih.gov/articles/PMC11847086/" class="view">Advanced delivery systems for gene editing: A comprehensive review from the GenE-HumDi COST Action Working Group</a></div><div class="supp"><div class="desc">Alessia Cavazza, Francisco J. Molina-Estévez, Álvaro Plaza Reyes, Victor Ronco, Asma Naseem, Špela Malenšek, Peter Pečan, Annalisa Santini, Paula Heredia, Araceli Aguilar-González, Houria Boulaiz, Qianqian Ni, Marina Cortijo-Gutierrez, Kristina Pavlovic, Inmaculada Herrera, Berta de la Cerda, Emilio M. Garcia-Tenorio, Eva Richard, Sergio Granados-Principal, Arístides López-Márquez, Mariana Köber, Marijana Stojanovic, Melita Vidaković, Irene Santos-Garcia, Lorea Blázquez, Emily Haughton, Dongnan Yan, Rosario María Sánchez-Martín, Loubna Mazini, Gloria Gonzalez Aseguinolaza, Annarita Miccio, Paula Rio, Lourdes R. Desviat, Manuel A.F.V. Gonçalves, Ling Peng, Cecilia Jiménez-Mallebrera, Francisco Martin Molina, Dhanu Gupta, Duško Lainšček, Yonglun Luo, Karim Benabdellah</div><div class="details"><b>Mol Ther Nucleic Acids</b>. <span class="citation-publication-date">2025 Mar 11; </span>36(1): 102457. <span class="">Published online 2025 Jan 17. </span><span class="doi"><span>doi: </span>10.1016/j.omtn.2025.102457</span></div></div><div class="aux"><div class="resc"><dl class="rprtid"><dt>PMCID: </dt><dd>PMC11847086</dd></dl></div></div><div class="aux"><div class="links"><a ref="ordinalpos=14&ncbi_uid=11847086&link_uid=11847086&linksrc=docsum_title" class="view" href="https://pmc.ncbi.nlm.nih.gov/articles/PMC11847086/">Article</a><a ref="ordinalpos=14&ncbi_uid=11847086&link_uid=11847086&linksrc=docsum_title" class="view" href="https://pmc.ncbi.nlm.nih.gov/articles/PMC11847086/pdf/main.pdf">PDF–4.2M</a></div></div></div></div><div class="rprt"><div class="rprtnum"><label for="UidCheckBox11834060" class="ui-helper-hidden-accessible">Select item 11834060</label><input name="EntrezSystem2.PEntrez.PMC.Pmc_ResultsPanel.Pmc_RVDocSum.uid" sid="15" type="checkbox" id="UidCheckBox11834060" value="11834060" /><span>15.</span></div><div class="rslt"><div class="title"><a ref="ordinalpos=15&ncbi_uid=11834060&link_uid=11834060&linksrc=docsum_title" href="https://pmc.ncbi.nlm.nih.gov/articles/PMC11834060/" class="view">Transcriptomic analysis of the immune response to <em>in vivo</em> gene electrotransfer in colorectal cancer</a></div><div class="supp"><div class="desc">Mariangela De Robertis, Tim Bozic, Iva Santek, Flaviana Marzano, Bostjan Markelc, Domenico Alessandro Silvestris, Apollonia Tullo, Graziano Pesole, Maja Cemazar, Emanuela Signori</div><div class="details"><b>Mol Ther Nucleic Acids</b>. <span class="citation-publication-date">2025 Mar 11; </span>36(1): 102448. <span class="">Published online 2025 Jan 16. </span><span class="doi"><span>doi: </span>10.1016/j.omtn.2025.102448</span></div></div><div class="aux"><div class="resc"><dl class="rprtid"><dt>PMCID: </dt><dd>PMC11834060</dd></dl></div></div><div class="aux"><div class="links"><a ref="ordinalpos=15&ncbi_uid=11834060&link_uid=11834060&linksrc=docsum_title" class="view" href="https://pmc.ncbi.nlm.nih.gov/articles/PMC11834060/">Article</a><a ref="ordinalpos=15&ncbi_uid=11834060&link_uid=11834060&linksrc=docsum_title" class="view" href="https://pmc.ncbi.nlm.nih.gov/articles/PMC11834060/pdf/main.pdf">PDF–3.7M</a></div></div></div></div><div class="rprt"><div class="rprtnum"><label for="UidCheckBox11835621" class="ui-helper-hidden-accessible">Select item 11835621</label><input name="EntrezSystem2.PEntrez.PMC.Pmc_ResultsPanel.Pmc_RVDocSum.uid" sid="16" type="checkbox" id="UidCheckBox11835621" value="11835621" /><span>16.</span></div><div class="rslt"><div class="title"><a ref="ordinalpos=16&ncbi_uid=11835621&link_uid=11835621&linksrc=docsum_title" href="https://pmc.ncbi.nlm.nih.gov/articles/PMC11835621/" class="view">Decoding CKD-induced muscle atrophy through the critical role of lncRNA GAS5 and pyroptosis</a></div><div class="supp"><div class="desc">Rong Huang, Xinying Tang, Shuang Liu, Lijing Sun</div><div class="details"><b>Mol Ther Nucleic Acids</b>. <span class="citation-publication-date">2025 Mar 11; </span>36(1): 102451. <span class="">Published online 2025 Jan 13. </span><span class="doi"><span>doi: </span>10.1016/j.omtn.2025.102451</span></div></div><div class="aux"><div class="resc"><dl class="rprtid"><dt>PMCID: </dt><dd>PMC11835621</dd></dl></div></div><div class="aux"><div class="links"><a ref="ordinalpos=16&ncbi_uid=11835621&link_uid=11835621&linksrc=docsum_title" class="view" href="https://pmc.ncbi.nlm.nih.gov/articles/PMC11835621/">Article</a><a ref="ordinalpos=16&ncbi_uid=11835621&link_uid=11835621&linksrc=docsum_title" class="view" href="https://pmc.ncbi.nlm.nih.gov/articles/PMC11835621/pdf/main.pdf">PDF–7.0M</a></div></div></div></div><div class="rprt"><div class="rprtnum"><label for="UidCheckBox11834102" class="ui-helper-hidden-accessible">Select item 11834102</label><input name="EntrezSystem2.PEntrez.PMC.Pmc_ResultsPanel.Pmc_RVDocSum.uid" sid="17" type="checkbox" id="UidCheckBox11834102" value="11834102" /><span>17.</span></div><div class="rslt"><div class="title"><a ref="ordinalpos=17&ncbi_uid=11834102&link_uid=11834102&linksrc=docsum_title" href="https://pmc.ncbi.nlm.nih.gov/articles/PMC11834102/" class="view">Development and characterization of a miRNA-responsive circular RNA expression system with cell type specificity</a></div><div class="supp"><div class="desc">Yu Ma, Yuqiao Mao, Shirui Luo, Wenjie Zuo, Peng Gao, Bo Ying</div><div class="details"><b>Mol Ther Nucleic Acids</b>. <span class="citation-publication-date">2025 Mar 11; </span>36(1): 102450. <span class="">Published online 2025 Jan 13. </span><span class="doi"><span>doi: </span>10.1016/j.omtn.2025.102450</span></div></div><div class="aux"><div class="resc"><dl class="rprtid"><dt>PMCID: </dt><dd>PMC11834102</dd></dl></div></div><div class="aux"><div class="links"><a ref="ordinalpos=17&ncbi_uid=11834102&link_uid=11834102&linksrc=docsum_title" class="view" href="https://pmc.ncbi.nlm.nih.gov/articles/PMC11834102/">Article</a><a ref="ordinalpos=17&ncbi_uid=11834102&link_uid=11834102&linksrc=docsum_title" class="view" href="https://pmc.ncbi.nlm.nih.gov/articles/PMC11834102/pdf/main.pdf">PDF–3.2M</a></div></div></div></div><div class="rprt"><div class="rprtnum"><label for="UidCheckBox11834087" class="ui-helper-hidden-accessible">Select item 11834087</label><input name="EntrezSystem2.PEntrez.PMC.Pmc_ResultsPanel.Pmc_RVDocSum.uid" sid="18" type="checkbox" id="UidCheckBox11834087" value="11834087" /><span>18.</span></div><div class="rslt"><div class="title"><a ref="ordinalpos=18&ncbi_uid=11834087&link_uid=11834087&linksrc=docsum_title" href="https://pmc.ncbi.nlm.nih.gov/articles/PMC11834087/" class="view">Use of polyadenosine tail mimetics to enhance mRNA expression from genes associated with haploinsufficiency disorders</a></div><div class="supp"><div class="desc">Bahareh Torkzaban, Yining Zhu, Christian Lopez, Jonathan M. Alexander, Jingyao Ma, Yongzhi Sun, Katharine R. Maschhoff, Wenqian Hu, Michele H. Jacob, Dingchang Lin, Hai-Quan Mao, Sophie Martin, Jeff Coller</div><div class="details"><b>Mol Ther Nucleic Acids</b>. <span class="citation-publication-date">2025 Mar 11; </span>36(1): 102453. <span class="">Published online 2025 Jan 13. </span><span class="doi"><span>doi: </span>10.1016/j.omtn.2025.102453</span></div></div><div class="aux"><div class="resc"><dl class="rprtid"><dt>PMCID: </dt><dd>PMC11834087</dd></dl></div></div><div class="aux"><div class="links"><a ref="ordinalpos=18&ncbi_uid=11834087&link_uid=11834087&linksrc=docsum_title" class="view" href="https://pmc.ncbi.nlm.nih.gov/articles/PMC11834087/">Article</a><a ref="ordinalpos=18&ncbi_uid=11834087&link_uid=11834087&linksrc=docsum_title" class="view" href="https://pmc.ncbi.nlm.nih.gov/articles/PMC11834087/pdf/main.pdf">PDF–4.1M</a></div></div></div></div><div class="rprt"><div class="rprtnum"><label for="UidCheckBox11803158" class="ui-helper-hidden-accessible">Select item 11803158</label><input name="EntrezSystem2.PEntrez.PMC.Pmc_ResultsPanel.Pmc_RVDocSum.uid" sid="19" type="checkbox" id="UidCheckBox11803158" value="11803158" /><span>19.</span></div><div class="rslt"><div class="title"><a ref="ordinalpos=19&ncbi_uid=11803158&link_uid=11803158&linksrc=docsum_title" href="https://pmc.ncbi.nlm.nih.gov/articles/PMC11803158/" class="view">Unveiling sequence-agnostic mixed-chemical modification patterns for splice-switching oligonucleotides using the NATURA platform</a></div><div class="supp"><div class="desc">Tommaso Tabaglio, Taniya Agarwal, Wei Yuan Cher, Jin Rong Ow, Ah Keng Chew, Priscila Yun Qian Sun, Raja Sekhar Reddy Gurrampati, Hongfang Lu, Praveena Naidu, Hong Kai Ng, Xavier Le Guezennec, Shi Yan Ng, Manikandan Lakshmanan, Ernesto Guccione, Keng Boon Wee</div><div class="details"><b>Mol Ther Nucleic Acids</b>. <span class="citation-publication-date">2025 Mar 11; </span>36(1): 102422. <span class="">Published online 2025 Jan 7. </span><span class="doi"><span>doi: </span>10.1016/j.omtn.2024.102422</span></div></div><div class="aux"><div class="resc"><dl class="rprtid"><dt>PMCID: </dt><dd>PMC11803158</dd></dl></div></div><div class="aux"><div class="links"><a ref="ordinalpos=19&ncbi_uid=11803158&link_uid=11803158&linksrc=docsum_title" class="view" href="https://pmc.ncbi.nlm.nih.gov/articles/PMC11803158/">Article</a><a ref="ordinalpos=19&ncbi_uid=11803158&link_uid=11803158&linksrc=docsum_title" class="view" href="https://pmc.ncbi.nlm.nih.gov/articles/PMC11803158/pdf/main.pdf">PDF–6.2M</a></div></div></div></div><div class="rprt"><div class="rprtnum"><label for="UidCheckBox11834101" class="ui-helper-hidden-accessible">Select item 11834101</label><input name="EntrezSystem2.PEntrez.PMC.Pmc_ResultsPanel.Pmc_RVDocSum.uid" sid="20" type="checkbox" id="UidCheckBox11834101" value="11834101" /><span>20.</span></div><div class="rslt"><div class="title"><a ref="ordinalpos=20&ncbi_uid=11834101&link_uid=11834101&linksrc=docsum_title" href="https://pmc.ncbi.nlm.nih.gov/articles/PMC11834101/" class="view">MSCs act as biopatches for blood-retinal barrier preservation to enhance functional recovery after retinal I/R</a></div><div class="supp"><div class="desc">Xiaoyue Wei, Hanyiqi Mu, Qinmu Zhang, Ziyuan Zhang, Yifei Ru, Kunbei Lai, Yuan Ma, Zhuangling Lin, Rebiya Tuxun, Zitong Chen, Andy Peng Xiang, Tao Li</div><div class="details"><b>Mol Ther Nucleic Acids</b>. <span class="citation-publication-date">2025 Mar 11; </span>36(1): 102445. <span class="">Published online 2025 Jan 2. </span><span class="doi"><span>doi: </span>10.1016/j.omtn.2024.102445</span></div></div><div class="aux"><div class="resc"><dl class="rprtid"><dt>PMCID: </dt><dd>PMC11834101</dd></dl></div></div><div class="aux"><div class="links"><a ref="ordinalpos=20&ncbi_uid=11834101&link_uid=11834101&linksrc=docsum_title" class="view" href="https://pmc.ncbi.nlm.nih.gov/articles/PMC11834101/">Article</a><a ref="ordinalpos=20&ncbi_uid=11834101&link_uid=11834101&linksrc=docsum_title" class="view" href="https://pmc.ncbi.nlm.nih.gov/articles/PMC11834101/pdf/main.pdf">PDF–5.4M</a></div></div></div></div></div>
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<textarea name="EntrezSystem2.PEntrez.PMC.Pmc_ResultsPanel.Discovery_SearchDetails.SearchDetailsTerm" sid="1" class="searchdetails_term" cols="30" rows="5" db="pmc">"Mol Ther Nucleic Acids"[jour]</textarea>
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||
</div>
|
||
</div>
|
||
<div class="row">
|
||
<div class="col-lg-12 centered-lg">
|
||
<nav class="bottom-links">
|
||
<ul class="mt-3">
|
||
<li>
|
||
<a class="text-white" href="//www.nlm.nih.gov/">NLM</a>
|
||
</li>
|
||
<li>
|
||
<a class="text-white" href="https://www.nih.gov/">NIH</a>
|
||
</li>
|
||
<li>
|
||
<a class="text-white" href="https://www.hhs.gov/">HHS</a>
|
||
</li>
|
||
<li>
|
||
<a class="text-white" href="https://www.usa.gov/">USA.gov</a>
|
||
</li>
|
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</ul>
|
||
</nav>
|
||
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||
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||
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|
||
</section>
|
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<script type="text/javascript" src="/portal/portal3rc.fcgi/static/js/hfjs2.js"> </script>
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