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Amyotrophic lateral sclerosis, susceptibility to

MedGen UID:
864751
Concept ID:
C4016314
Finding
Synonym: AMYOTROPHIC LATERAL SCLEROSIS, SUSCEPTIBILITY TO
 
OMIM®: 162230; 170710; 601143

Professional guidelines

PubMed

Daria T, Müller K, Oidovdorj G, Baatar K, Boldbaatar P, Sarangerel J, Rentsenbat M, Turbat S, Yadamsuren E, Weydt P, Dambasuren B, Bosookhuu O, Banzrai C, Damchaa B, Pinkhardt EH, Rosenbohm A, Högel J, Andersen P, Borck G, Batmunkh M, Ludolph AC, Weishaupt JH
J Neurol Neurosurg Psychiatry 2019 Nov;90(11):1300-1302. Epub 2019 Jul 29 doi: 10.1136/jnnp-2019-320640. PMID: 31358569
Nakken O, Sørum L, Holmøy T
Tidsskr Nor Laegeforen 2018 Sep 4;138(13) Epub 2018 Sep 3 doi: 10.4045/tidsskr.18.0193. PMID: 30180501
Byrne S, Bede P, Elamin M, Kenna K, Lynch C, McLaughlin R, Hardiman O
Amyotroph Lateral Scler 2011 May;12(3):157-9. Epub 2011 Jan 5 doi: 10.3109/17482968.2010.545420. PMID: 21208036

Recent clinical studies

Etiology

Irwin KE, Sheth U, Wong PC, Gendron TF
Mol Neurodegener 2024 Jan 24;19(1):9. doi: 10.1186/s13024-023-00685-6. PMID: 38267984Free PMC Article
Van Daele SH, Moisse M, van Vugt JJFA, Zwamborn RAJ, van der Spek R, van Rheenen W, Van Eijk K, Kenna K, Corcia P, Vourc'h P, Couratier P, Hardiman O, McLaughin R, Gotkine M, Drory V, Ticozzi N, Silani V, Ratti A, de Carvalho M, Mora Pardina JS, Povedano M, Andersen PM, Weber M, Başak NA, Shaw C, Shaw PJ, Morrison KE, Landers JE, Glass JD, van Es MA, van den Berg LH, Al-Chalabi A, Veldink J, Van Damme P
Brain 2023 Sep 1;146(9):3760-3769. doi: 10.1093/brain/awad120. PMID: 37043475Free PMC Article
Cookson MR
Adv Neurobiol 2017;15:479-489. doi: 10.1007/978-3-319-57193-5_19. PMID: 28674994
Talbott EO, Malek AM, Lacomis D
Handb Clin Neurol 2016;138:225-38. doi: 10.1016/B978-0-12-802973-2.00013-6. PMID: 27637961
Cirulli ET, Lasseigne BN, Petrovski S, Sapp PC, Dion PA, Leblond CS, Couthouis J, Lu YF, Wang Q, Krueger BJ, Ren Z, Keebler J, Han Y, Levy SE, Boone BE, Wimbish JR, Waite LL, Jones AL, Carulli JP, Day-Williams AG, Staropoli JF, Xin WW, Chesi A, Raphael AR, McKenna-Yasek D, Cady J, Vianney de Jong JM, Kenna KP, Smith BN, Topp S, Miller J, Gkazi A; FALS Sequencing Consortium, Al-Chalabi A, van den Berg LH, Veldink J, Silani V, Ticozzi N, Shaw CE, Baloh RH, Appel S, Simpson E, Lagier-Tourenne C, Pulst SM, Gibson S, Trojanowski JQ, Elman L, McCluskey L, Grossman M, Shneider NA, Chung WK, Ravits JM, Glass JD, Sims KB, Van Deerlin VM, Maniatis T, Hayes SD, Ordureau A, Swarup S, Landers J, Baas F, Allen AS, Bedlack RS, Harper JW, Gitler AD, Rouleau GA, Brown R, Harms MB, Cooper GM, Harris T, Myers RM, Goldstein DB
Science 2015 Mar 27;347(6229):1436-41. Epub 2015 Feb 19 doi: 10.1126/science.aaa3650. PMID: 25700176Free PMC Article

Diagnosis

Nijs M, Van Damme P
Curr Opin Neurol 2024 Oct 1;37(5):560-569. Epub 2024 Aug 22 doi: 10.1097/WCO.0000000000001294. PMID: 38967083Free PMC Article
Mirzalieva O, Juncker M, Schwartzenburg J, Desai S
Cells 2022 Feb 4;11(3) doi: 10.3390/cells11030538. PMID: 35159348Free PMC Article
van Es MA, Hardiman O, Chio A, Al-Chalabi A, Pasterkamp RJ, Veldink JH, van den Berg LH
Lancet 2017 Nov 4;390(10107):2084-2098. Epub 2017 May 25 doi: 10.1016/S0140-6736(17)31287-4. PMID: 28552366
Talbott EO, Malek AM, Lacomis D
Handb Clin Neurol 2016;138:225-38. doi: 10.1016/B978-0-12-802973-2.00013-6. PMID: 27637961
Rowland LP, Shneider NA
N Engl J Med 2001 May 31;344(22):1688-700. doi: 10.1056/NEJM200105313442207. PMID: 11386269

Therapy

Jiang Z, Gu XJ, Su WM, Duan QQ, Yin KF, Ren YL, Wang Y, Cao B, Chen YP
Mol Neurobiol 2024 Sep;61(9):6572-6583. Epub 2024 Feb 7 doi: 10.1007/s12035-024-04007-9. PMID: 38324182
Irwin KE, Sheth U, Wong PC, Gendron TF
Mol Neurodegener 2024 Jan 24;19(1):9. doi: 10.1186/s13024-023-00685-6. PMID: 38267984Free PMC Article
Tian Y, Ma G, Li H, Zeng Y, Zhou S, Wang X, Shan S, Xu Y, Xiong J, Cheng G
Mov Disord 2023 Oct;38(10):1813-1821. Epub 2023 Aug 3 doi: 10.1002/mds.29572. PMID: 37534731
Zhang W, Xiao D, Mao Q, Xia H
Signal Transduct Target Ther 2023 Jul 12;8(1):267. doi: 10.1038/s41392-023-01486-5. PMID: 37433768Free PMC Article
Sivandzade F, Prasad S, Bhalerao A, Cucullo L
Redox Biol 2019 Feb;21:101059. Epub 2018 Nov 28 doi: 10.1016/j.redox.2018.11.017. PMID: 30576920Free PMC Article

Prognosis

Irwin KE, Sheth U, Wong PC, Gendron TF
Mol Neurodegener 2024 Jan 24;19(1):9. doi: 10.1186/s13024-023-00685-6. PMID: 38267984Free PMC Article
Mirzalieva O, Juncker M, Schwartzenburg J, Desai S
Cells 2022 Feb 4;11(3) doi: 10.3390/cells11030538. PMID: 35159348Free PMC Article
Berdyński M, Miszta P, Safranow K, Andersen PM, Morita M, Filipek S, Żekanowski C, Kuźma-Kozakiewicz M
Sci Rep 2022 Jan 7;12(1):103. doi: 10.1038/s41598-021-03891-8. PMID: 34996976Free PMC Article
van Es MA, Hardiman O, Chio A, Al-Chalabi A, Pasterkamp RJ, Veldink JH, van den Berg LH
Lancet 2017 Nov 4;390(10107):2084-2098. Epub 2017 May 25 doi: 10.1016/S0140-6736(17)31287-4. PMID: 28552366
Checkoway H, Lundin JI, Kelada SN
IARC Sci Publ 2011;(163):407-19. PMID: 22997874

Clinical prediction guides

Irwin KE, Sheth U, Wong PC, Gendron TF
Mol Neurodegener 2024 Jan 24;19(1):9. doi: 10.1186/s13024-023-00685-6. PMID: 38267984Free PMC Article
Baj J, Flieger W, Barbachowska A, Kowalska B, Flieger M, Forma A, Teresiński G, Portincasa P, Buszewicz G, Radzikowska-Büchner E, Flieger J
Int J Mol Sci 2023 Oct 6;24(19) doi: 10.3390/ijms241914959. PMID: 37834407Free PMC Article
Tian Y, Ma G, Li H, Zeng Y, Zhou S, Wang X, Shan S, Xu Y, Xiong J, Cheng G
Mov Disord 2023 Oct;38(10):1813-1821. Epub 2023 Aug 3 doi: 10.1002/mds.29572. PMID: 37534731
McCauley ME, O'Rourke JG, Yáñez A, Markman JL, Ho R, Wang X, Chen S, Lall D, Jin M, Muhammad AKMG, Bell S, Landeros J, Valencia V, Harms M, Arditi M, Jefferies C, Baloh RH
Nature 2020 Sep;585(7823):96-101. Epub 2020 Aug 19 doi: 10.1038/s41586-020-2625-x. PMID: 32814898Free PMC Article
Cirulli ET, Lasseigne BN, Petrovski S, Sapp PC, Dion PA, Leblond CS, Couthouis J, Lu YF, Wang Q, Krueger BJ, Ren Z, Keebler J, Han Y, Levy SE, Boone BE, Wimbish JR, Waite LL, Jones AL, Carulli JP, Day-Williams AG, Staropoli JF, Xin WW, Chesi A, Raphael AR, McKenna-Yasek D, Cady J, Vianney de Jong JM, Kenna KP, Smith BN, Topp S, Miller J, Gkazi A; FALS Sequencing Consortium, Al-Chalabi A, van den Berg LH, Veldink J, Silani V, Ticozzi N, Shaw CE, Baloh RH, Appel S, Simpson E, Lagier-Tourenne C, Pulst SM, Gibson S, Trojanowski JQ, Elman L, McCluskey L, Grossman M, Shneider NA, Chung WK, Ravits JM, Glass JD, Sims KB, Van Deerlin VM, Maniatis T, Hayes SD, Ordureau A, Swarup S, Landers J, Baas F, Allen AS, Bedlack RS, Harper JW, Gitler AD, Rouleau GA, Brown R, Harms MB, Cooper GM, Harris T, Myers RM, Goldstein DB
Science 2015 Mar 27;347(6229):1436-41. Epub 2015 Feb 19 doi: 10.1126/science.aaa3650. PMID: 25700176Free PMC Article

Recent systematic reviews

Teruel-Peña B, Gómez-Urquiza JL, Suleiman-Martos N, Prieto I, García-Cózar FJ, Ramírez-Sánchez M, Fernández-Martos C, Domínguez-Vías G
Int J Mol Sci 2023 Apr 12;24(8) doi: 10.3390/ijms24087169. PMID: 37108335Free PMC Article
Silva-Moraes MH, Bispo-Torres AC, Barouh JL, Lucena PH, Armani-Franceschi G, Dorea-Bandeira I, Vieira F, Miranda-Scippa Â, Quarantini LC, Lucena R, Bandeira ID
J Affect Disord 2020 Dec 1;277:688-696. Epub 2020 Sep 1 doi: 10.1016/j.jad.2020.08.066. PMID: 32911219
Srinivasan E, Rajasekaran R
J Mol Neurosci 2020 Nov;70(11):1742-1770. Epub 2020 May 15 doi: 10.1007/s12031-020-01569-w. PMID: 32415434
Zhou SL, Tan CC, Hou XH, Cao XP, Tan L, Yu JT
J Alzheimers Dis 2019;68(3):1171-1184. doi: 10.3233/JAD-181038. PMID: 30883352
Zou ZY, Zhou ZR, Che CH, Liu CY, He RL, Huang HP
J Neurol Neurosurg Psychiatry 2017 Jul;88(7):540-549. Epub 2017 Jan 5 doi: 10.1136/jnnp-2016-315018. PMID: 28057713

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