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Choroidal Dystrophy

MedGen UID:
149097
Concept ID:
C0730291
Disease or Syndrome
Synonym: Choroidal dystrophy
SNOMED CT: Choroidal dystrophy (312918002)

Professional guidelines

PubMed

Buhler VMM, Berger L, Schaller A, Zinkernagel MS, Wolf S, Escher P
Genes (Basel) 2021 May 26;12(6) doi: 10.3390/genes12060812. PMID: 34073554Free PMC Article
Kersten E, Geerlings MJ, Pauper M, Corominas J, Bakker B, Altay L, Fauser S, de Jong EK, Hoyng CB, den Hollander AI
Clin Genet 2018 Dec;94(6):569-574. Epub 2018 Oct 15 doi: 10.1111/cge.13447. PMID: 30215852Free PMC Article

Recent clinical studies

Etiology

Heath Jeffery RC, Thompson JA, Lo J, Chelva ES, Armstrong S, Pulido JS, Procopio R, Vincent AL, Bianco L, Battaglia Parodi M, Ziccardi L, Antonelli G, Barbano L, Marques JP, Geada S, Carvalho AL, Tang WC, Chan CM, Boon CJF, Hensman J, Chen TC, Lin CY, Chen PL, Vincent A, Tumber A, Heon E, Grigg JR, Jamieson RV, Cornish EE, Nash BM, Borooah S, Ayton LN, Britten-Jones AC, Edwards TL, Ruddle JB, Sharma A, Porter RG, Lamey TM, McLaren TL, McLenachan S, Roshandel D, Chen FK
Invest Ophthalmol Vis Sci 2024 May 1;65(5):22. doi: 10.1167/iovs.65.5.22. PMID: 38743414Free PMC Article
Ruiz-Pastor MJ, Sánchez-Sáez X, Kutsyr O, Albertos-Arranz H, Sánchez-Castillo C, Ortuño-Lizarán I, Martínez-Gil N, Vidal-Gil L, Méndez L, Sánchez-Martín M, Maneu V, Lax P, Cuenca N
Cell Death Dis 2023 Nov 1;14(11):711. doi: 10.1038/s41419-023-06243-8. PMID: 37914688Free PMC Article
Weisschuh N, Obermaier CD, Battke F, Bernd A, Kuehlewein L, Nasser F, Zobor D, Zrenner E, Weber E, Wissinger B, Biskup S, Stingl K, Kohl S
Hum Mutat 2020 Sep;41(9):1514-1527. Epub 2020 Jun 29 doi: 10.1002/humu.24064. PMID: 32531858
Bax NM, Valkenburg D, Lambertus S, Klevering BJ, Boon CJF, Holz FG, Cremers FPM, Fleckenstein M, Hoyng CB, Lindner M; Foveal Sparing Atrophy Study Team (FAST)
Invest Ophthalmol Vis Sci 2019 Aug 1;60(10):3456-3467. doi: 10.1167/iovs.18-26533. PMID: 31398255
Forte R, Aptel F, Feldmann A, Chiquet C
Retin Cases Brief Rep 2018 Winter;12(1):29-32. doi: 10.1097/ICB.0000000000000400. PMID: 27579567

Diagnosis

Bommakanti N, Besirli CG, Zhao PY
JAMA Ophthalmol 2023 Jan 1;141(1):102-104. doi: 10.1001/jamaophthalmol.2022.5269. PMID: 36480192
Weisschuh N, Obermaier CD, Battke F, Bernd A, Kuehlewein L, Nasser F, Zobor D, Zrenner E, Weber E, Wissinger B, Biskup S, Stingl K, Kohl S
Hum Mutat 2020 Sep;41(9):1514-1527. Epub 2020 Jun 29 doi: 10.1002/humu.24064. PMID: 32531858
Gala JM, Narayanan R
BMJ Case Rep 2019 Oct 23;12(10) doi: 10.1136/bcr-2019-230495. PMID: 31645393Free PMC Article
Ghodasra DH, Besirli C
JAMA Ophthalmol 2015 Dec;133(12):e152148. Epub 2015 Dec 10 doi: 10.1001/jamaophthalmol.2015.2148. PMID: 26659444
Greve EL, Furuno F
Albrecht Von Graefes Arch Klin Exp Ophthalmol 1980;213(1):33-41. doi: 10.1007/BF02391209. PMID: 6906144

Therapy

da Palma MM, Ku C, Igelman AD, Burr A, Shevchenko Sutherland L, Koerner C, Valle D, Pennesi ME, Yang P
Ophthalmic Genet 2023 Apr;44(2):191-197. Epub 2022 Jul 20 doi: 10.1080/13816810.2022.2098986. PMID: 35856163
Smailhodzic D, Fleckenstein M, Theelen T, Boon CJ, van Huet RA, van de Ven JP, Den Hollander AI, Schmitz-Valckenberg S, Hoyng CB, Weber BH, Holz FG, Klevering BJ
Invest Ophthalmol Vis Sci 2011 Nov 21;52(12):8908-18. doi: 10.1167/iovs.11-7926. PMID: 22003107
Chisholm IH, Gass JD, Hutton WL
Am J Ophthalmol 1976 Sep;82(3):343-51. doi: 10.1016/0002-9394(76)90482-7. PMID: 961787

Prognosis

Bax NM, Valkenburg D, Lambertus S, Klevering BJ, Boon CJF, Holz FG, Cremers FPM, Fleckenstein M, Hoyng CB, Lindner M; Foveal Sparing Atrophy Study Team (FAST)
Invest Ophthalmol Vis Sci 2019 Aug 1;60(10):3456-3467. doi: 10.1167/iovs.18-26533. PMID: 31398255
Kersten E, Geerlings MJ, Pauper M, Corominas J, Bakker B, Altay L, Fauser S, de Jong EK, Hoyng CB, den Hollander AI
Clin Genet 2018 Dec;94(6):569-574. Epub 2018 Oct 15 doi: 10.1111/cge.13447. PMID: 30215852Free PMC Article
Forte R, Aptel F, Feldmann A, Chiquet C
Retin Cases Brief Rep 2018 Winter;12(1):29-32. doi: 10.1097/ICB.0000000000000400. PMID: 27579567
Boon CJ, Klevering BJ, Cremers FP, Zonneveld-Vrieling MN, Theelen T, Den Hollander AI, Hoyng CB
Ophthalmology 2009 Apr;116(4):771-82, 782.e1. Epub 2009 Feb 25 doi: 10.1016/j.ophtha.2008.12.019. PMID: 19243827
Greve EL, Furuno F
Albrecht Von Graefes Arch Klin Exp Ophthalmol 1980;213(1):33-41. doi: 10.1007/BF02391209. PMID: 6906144

Clinical prediction guides

Heath Jeffery RC, Thompson JA, Lo J, Chelva ES, Armstrong S, Pulido JS, Procopio R, Vincent AL, Bianco L, Battaglia Parodi M, Ziccardi L, Antonelli G, Barbano L, Marques JP, Geada S, Carvalho AL, Tang WC, Chan CM, Boon CJF, Hensman J, Chen TC, Lin CY, Chen PL, Vincent A, Tumber A, Heon E, Grigg JR, Jamieson RV, Cornish EE, Nash BM, Borooah S, Ayton LN, Britten-Jones AC, Edwards TL, Ruddle JB, Sharma A, Porter RG, Lamey TM, McLaren TL, McLenachan S, Roshandel D, Chen FK
Invest Ophthalmol Vis Sci 2024 May 1;65(5):22. doi: 10.1167/iovs.65.5.22. PMID: 38743414Free PMC Article
Ruiz-Pastor MJ, Sánchez-Sáez X, Kutsyr O, Albertos-Arranz H, Sánchez-Castillo C, Ortuño-Lizarán I, Martínez-Gil N, Vidal-Gil L, Méndez L, Sánchez-Martín M, Maneu V, Lax P, Cuenca N
Cell Death Dis 2023 Nov 1;14(11):711. doi: 10.1038/s41419-023-06243-8. PMID: 37914688Free PMC Article
Forte R, Aptel F, Feldmann A, Chiquet C
Retin Cases Brief Rep 2018 Winter;12(1):29-32. doi: 10.1097/ICB.0000000000000400. PMID: 27579567
Boon CJ, Klevering BJ, Cremers FP, Zonneveld-Vrieling MN, Theelen T, Den Hollander AI, Hoyng CB
Ophthalmology 2009 Apr;116(4):771-82, 782.e1. Epub 2009 Feb 25 doi: 10.1016/j.ophtha.2008.12.019. PMID: 19243827
Greve EL, Furuno F
Albrecht Von Graefes Arch Klin Exp Ophthalmol 1980;213(1):33-41. doi: 10.1007/BF02391209. PMID: 6906144

Recent systematic reviews

Bassil FL, Colijn JM, Thiadens AAHJ, Biarnés M
Am J Ophthalmol 2025 Jan;269:30-48. Epub 2024 Aug 15 doi: 10.1016/j.ajo.2024.07.035. PMID: 39153684

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