U.S. flag

An official website of the United States government

Format

Send to:

Choose Destination

Gm2-gangliosidosis, adult

MedGen UID:
853856
Concept ID:
C2874270
Disease or Syndrome
Synonym: GM2-GANGLIOSIDOSIS, ADULT
 
OMIM®: 606869

Professional guidelines

PubMed

Mansouri V, Tavasoli AR, Khodarahmi M, Dakkali MS, Daneshfar S, Ashrafi MR, Heidari M, Hosseinpour S, Sharifianjazi F, Bemanalizadeh M
Eur J Neurol 2023 Sep;30(9):2919-2945. Epub 2023 Jun 8 doi: 10.1111/ene.15871. PMID: 37209042
Strom CM
MLO Med Lab Obs 2004 Aug;36(8):12-7; quiz 20-1. PMID: 15366363
Simpson JL, Verp MS
Clin Obstet Gynecol 1982 Dec;25(4):635-58. doi: 10.1097/00003081-198212000-00004. PMID: 6761024

Recent clinical studies

Etiology

Mansouri V, Tavasoli AR, Khodarahmi M, Dakkali MS, Daneshfar S, Ashrafi MR, Heidari M, Hosseinpour S, Sharifianjazi F, Bemanalizadeh M
Eur J Neurol 2023 Sep;30(9):2919-2945. Epub 2023 Jun 8 doi: 10.1111/ene.15871. PMID: 37209042
Ensenauer RE, Michels VV, Reinke SS
Mayo Clin Proc 2005 Jan;80(1):63-73. doi: 10.1016/S0025-6196(11)62960-1. PMID: 15667031
Janz NK, Becker MH
Health Educ Q 1984 Spring;11(1):1-47. doi: 10.1177/109019818401100101. PMID: 6392204
Simpson JL, Verp MS
Clin Obstet Gynecol 1982 Dec;25(4):635-58. doi: 10.1097/00003081-198212000-00004. PMID: 6761024
Neufeld HN, Schneeweiss A
Clin Cardiol 1981 Sep-Oct;4(5):217-22. doi: 10.1002/clc.4960040501. PMID: 7030562

Diagnosis

Mansouri V, Tavasoli AR, Khodarahmi M, Dakkali MS, Daneshfar S, Ashrafi MR, Heidari M, Hosseinpour S, Sharifianjazi F, Bemanalizadeh M
Eur J Neurol 2023 Sep;30(9):2919-2945. Epub 2023 Jun 8 doi: 10.1111/ene.15871. PMID: 37209042
Strom CM
MLO Med Lab Obs 2004 Aug;36(8):12-7; quiz 20-1. PMID: 15366363
Federico A, Palmeri S, Malandrini A, Fabrizi G, Mondelli M, Guazzi GC
Dev Neurosci 1991;13(4-5):280-7. doi: 10.1159/000112174. PMID: 1840098
Longdon K, Pennock CA
Ann Clin Biochem 1979 May;16(3):152-4. doi: 10.1177/000456327901600132. PMID: 160211
Niedermeyer E, Fineyre F, Riley T, Bird B
Clin Electroencephalogr 1979 Apr;10(2):75-95. doi: 10.1177/155005947901000206. PMID: 110503

Therapy

Mansouri V, Tavasoli AR, Khodarahmi M, Dakkali MS, Daneshfar S, Ashrafi MR, Heidari M, Hosseinpour S, Sharifianjazi F, Bemanalizadeh M
Eur J Neurol 2023 Sep;30(9):2919-2945. Epub 2023 Jun 8 doi: 10.1111/ene.15871. PMID: 37209042
Martakis K, Claassen J, Gascon-Bayari J, Goldschagg N, Hahn A, Hassan A, Hennig A, Jones S, Kay R, Lau H, Perlman S, Sharma R, Schneider S, Bremova-Ertl T
Neurology 2023 Mar 7;100(10):e1072-e1083. Epub 2022 Dec 1 doi: 10.1212/WNL.0000000000201660. PMID: 36456200Free PMC Article
Regier DS, Proia RL, D'Azzo A, Tifft CJ
Pediatr Endocrinol Rev 2016 Jun;13 Suppl 1(Suppl 1):663-73. PMID: 27491214Free PMC Article
Janz NK, Becker MH
Health Educ Q 1984 Spring;11(1):1-47. doi: 10.1177/109019818401100101. PMID: 6392204
Simpson JL, Verp MS
Clin Obstet Gynecol 1982 Dec;25(4):635-58. doi: 10.1097/00003081-198212000-00004. PMID: 6761024

Prognosis

Kern J, Böhringer J, Timmann D, Trollmann R, Stendel C, Kamm C, Röbl M, Santhanakumaran V, Groeschel S, Beck-Wödl S, Göricke S, Krägeloh-Mann I, Synofzik M
Neurology 2024 Jan 9;102(1):e207898. Epub 2023 Dec 12 doi: 10.1212/WNL.0000000000207898. PMID: 38165373Free PMC Article
Masingue M, Dufour L, Lenglet T, Saleille L, Goizet C, Ayrignac X, Ory-Magne F, Barth M, Lamari F, Mandia D, Caillaud C, Nadjar Y
Ann Neurol 2020 Apr;87(4):609-617. Epub 2020 Feb 7 doi: 10.1002/ana.25689. PMID: 31995250
Giraud C, Dussau J, Azouguene E, Feillet F, Puech JP, Caillaud C
Biochem Biophys Res Commun 2010 Feb 19;392(4):599-602. Epub 2010 Jan 25 doi: 10.1016/j.bbrc.2010.01.088. PMID: 20100466
Ben-Zeev B, Gross V, Kushnir T, Shalev R, Hoffman C, Shinar Y, Pras E, Brand N
J Child Neurol 2001 Feb;16(2):93-9. doi: 10.1177/088307380101600205. PMID: 11292232
Bach G, Tomczak J, Risch N, Ekstein J
Am J Med Genet 2001 Feb 15;99(1):70-5. doi: 10.1002/1096-8628(20010215)99:1<70::aid-ajmg1120>3.0.co;2-0. PMID: 11170098

Clinical prediction guides

Kissell J, Rochmann C, Minini P, Eichler F, Stephen CD, Lau H, Toro C, Johnston JM, Krupnick R, Hamed A, Cox GF
Mol Genet Metab 2024 Jul;142(3):108512. Epub 2024 Jun 6 doi: 10.1016/j.ymgme.2024.108512. PMID: 38870773Free PMC Article
Kern J, Böhringer J, Timmann D, Trollmann R, Stendel C, Kamm C, Röbl M, Santhanakumaran V, Groeschel S, Beck-Wödl S, Göricke S, Krägeloh-Mann I, Synofzik M
Neurology 2024 Jan 9;102(1):e207898. Epub 2023 Dec 12 doi: 10.1212/WNL.0000000000207898. PMID: 38165373Free PMC Article
Mansouri V, Tavasoli AR, Khodarahmi M, Dakkali MS, Daneshfar S, Ashrafi MR, Heidari M, Hosseinpour S, Sharifianjazi F, Bemanalizadeh M
Eur J Neurol 2023 Sep;30(9):2919-2945. Epub 2023 Jun 8 doi: 10.1111/ene.15871. PMID: 37209042
Osmon KJ, Thompson P, Woodley E, Karumuthil-Melethil S, Heindel C, Keimel JG, Kaemmerer WF, Gray SJ, Walia JS
Curr Gene Ther 2022;22(3):262-276. doi: 10.2174/1566523221666210916153051. PMID: 34530708
Austein CF, Seashore MR, Mick SS
Yale J Biol Med 1981 Sep-Oct;54(5):345-54. PMID: 7336765Free PMC Article

Recent systematic reviews

Mansouri V, Tavasoli AR, Khodarahmi M, Dakkali MS, Daneshfar S, Ashrafi MR, Heidari M, Hosseinpour S, Sharifianjazi F, Bemanalizadeh M
Eur J Neurol 2023 Sep;30(9):2919-2945. Epub 2023 Jun 8 doi: 10.1111/ene.15871. PMID: 37209042
Ysselstein D, Shulman JM, Krainc D
Mov Disord 2019 May;34(5):614-624. Epub 2019 Feb 6 doi: 10.1002/mds.27631. PMID: 30726573Free PMC Article
Lew RM, Burnett L, Proos AL, Barlow-Stewart K, Delatycki MB, Bankier A, Aizenberg H, Field MJ, Berman Y, Fleischer R, Fietz M
J Paediatr Child Health 2015 Mar;51(3):271-9. Epub 2014 Jun 13 doi: 10.1111/jpc.12632. PMID: 24923490

Supplemental Content

Table of contents

    Clinical resources

    Practice guidelines

    • PubMed
      See practice and clinical guidelines in PubMed. The search results may include broader topics and may not capture all published guidelines. See the FAQ for details.

    Consumer resources

    Recent activity

    Your browsing activity is empty.

    Activity recording is turned off.

    Turn recording back on

    See more...