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Polysaccharide, storage of unusual

MedGen UID:
376645
Concept ID:
C1849721
Pathologic Function
Synonym: Polysaccharide, Storage of Unusual
 
Monarch Initiative: MONDO:0009898
OMIM®: 263600

Clinical features

From HPO
Abnormal circulating polysaccharide concentration
MedGen UID:
1684710
Concept ID:
C5139057
Finding
A deviation from the normal concentration of a polysaccharide in the blood circulation.

Recent clinical studies

Etiology

An Y, Young SP, Hillman SL, Van Hove JL, Chen YT, Millington DS
Anal Biochem 2000 Dec 1;287(1):136-43. doi: 10.1006/abio.2000.4838. PMID: 11078593
Kiehl P, Metze D, Kresse H, Reimann S, Kraft D, Kapp A
Br J Dermatol 1998 Apr;138(4):672-7. doi: 10.1046/j.1365-2133.1998.02184.x. PMID: 9640378
Stejskalová A, Stejskal J, Elleder M
Czech Med 1987;10(4):201-16. PMID: 2449318
Yunis JJ, Lewandowski RC Jr, Sanfilippo SJ, Tsai MY, Foni I, Bruhl HH
Am J Med 1976 Dec;61(6):841-8. doi: 10.1016/0002-9343(76)90408-3. PMID: 1008071

Diagnosis

Oudesluijs G, Simon ME, Burggraaf RH, Waterham HR, Hennekam RC
Am J Med Genet A 2012 Feb;158A(2):292-7. Epub 2011 Dec 2 doi: 10.1002/ajmg.a.34396. PMID: 22140078
An Y, Young SP, Hillman SL, Van Hove JL, Chen YT, Millington DS
Anal Biochem 2000 Dec 1;287(1):136-43. doi: 10.1006/abio.2000.4838. PMID: 11078593
Tse HF, Shek TW, Tai YT, Lau YK, Ma L
Am J Med Sci 1996 Oct;312(4):182-6. doi: 10.1097/00000441-199610000-00006. PMID: 8853067
Gray F, Gherardi R, Marshall A, Janota I, Poirier J
J Neuropathol Exp Neurol 1988 Jul;47(4):459-74. doi: 10.1097/00005072-198807000-00007. PMID: 2838589
Yunis JJ, Lewandowski RC Jr, Sanfilippo SJ, Tsai MY, Foni I, Bruhl HH
Am J Med 1976 Dec;61(6):841-8. doi: 10.1016/0002-9343(76)90408-3. PMID: 1008071

Therapy

Ebrahimzadeh Leylabadlo H, Ghotaslou R, Samadi Kafil H, Feizabadi MM, Moaddab SY, Farajnia S, Sheykhsaran E, Sanaie S, Shanehbandi D, Bannazadeh Baghi H
Eur J Clin Microbiol Infect Dis 2020 Apr;39(4):613-627. Epub 2019 Dec 11 doi: 10.1007/s10096-019-03746-1. PMID: 31828683
Kiehl P, Metze D, Kresse H, Reimann S, Kraft D, Kapp A
Br J Dermatol 1998 Apr;138(4):672-7. doi: 10.1046/j.1365-2133.1998.02184.x. PMID: 9640378
Stejskalová A, Stejskal J, Elleder M
Czech Med 1987;10(4):201-16. PMID: 2449318

Prognosis

Sampson JB, Chin SS, Clayton FC, Pestronk A, Swoboda KJ, Flanigan KM
Neuromuscul Disord 2006 Jun;16(6):391-3. Epub 2006 May 11 doi: 10.1016/j.nmd.2006.03.013. PMID: 16697198
Slonim AE, Bulone L, Minikes J, Hays AP, Shanske S, Tsujino S, DiMauro S
Muscle Nerve 2006 Apr;33(4):571-4. doi: 10.1002/mus.20473. PMID: 16320310
Hinek A, Teitell MA, Schoyer L, Allen W, Gripp KW, Hamilton R, Weksberg R, Klüppel M, Lin AE
Am J Med Genet A 2005 Feb 15;133A(1):1-12. doi: 10.1002/ajmg.a.30495. PMID: 15637729
van der Ploeg AT, Kroos M, van Dongen JM, Visser WJ, Bolhuis PA, Loonen MC, Reuser AJ
J Neurol Sci 1987 Jul;79(3):327-36. doi: 10.1016/0022-510x(87)90239-5. PMID: 3302116
Yunis JJ, Lewandowski RC Jr, Sanfilippo SJ, Tsai MY, Foni I, Bruhl HH
Am J Med 1976 Dec;61(6):841-8. doi: 10.1016/0002-9343(76)90408-3. PMID: 1008071

Clinical prediction guides

Bailly M, Germain N, Féasson L, Costes F, Estour B, Hourdé C, N Merlet A, Thomas T, Hager J, Pereira B, Thivel D, Courteix D, Galusca B, Verney J
Appl Physiol Nutr Metab 2020 Nov;45(11):1287-1298. Epub 2020 Jun 1 doi: 10.1139/apnm-2020-0068. PMID: 32479741
Hecht JT, Makitie O, Hayes E, Haynes R, Susic M, Montufar-Solis D, Duke PJ, Cole WG
J Orthop Res 2004 Jul;22(4):759-67. doi: 10.1016/j.orthres.2003.11.010. PMID: 15183431
Hamilton S, Odili J, Pacifico MD, Wilson GD, Kupsch JM
Hybrid Hybridomics 2003 Dec;22(6):347-55. doi: 10.1089/153685903771797048. PMID: 14683594
Eishi Y, Takemura T, Sone R, Yamamura H, Narisawa K, Ichinohasama R, Tanaka M, Hatakeyama S
Hum Pathol 1985 Feb;16(2):193-7. doi: 10.1016/s0046-8177(85)80071-x. PMID: 3918928
Porte A, Stoeckel ME, Sacrez A, Batzenschlager A
Virchows Arch A Pathol Anat Histol 1980;386(1):43-58. doi: 10.1007/BF00432643. PMID: 7405006

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